BL 125858
BL 125858
U.S. License Holder:
Ultragenyx Pharmaceutical Inc.
Date of License:
August-19-2026
Last Update:
September-15-2026
FDA-Approved IndicationsGENGLYCOS (pariglasgene brecaparvovec-opnr) is an adeno-associated virus (AAV) vector-based gene therapy indicated to reduce daily cornstarch intake as an adjunct to nutritional management in adult and pediatric patients 8 years of age and older with glycogen storage disease type Ia (GSDIa).
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